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: Treosulfan Therapeutic Drug Monitoring: Optimizing Conditioning Therapy in Pediatric Hematopoietic Stem Cell Transplantation

Researchers

Presenter

  • Francesco Delle Cave

Principal Investigators

  • Simona De Gregori

  • Sonia Bonanomi

  • Adriana Balduzzi

  • Natalia Maximova

  • Marco Rabusin

  • Maria Ester Bernardo

  • Sabrina Basso

  • Giovanna Giorgiani

  • Lauren Marguerite Kelly

  • Marco Zecca

Medical Centers

  • Clinica Pediatrica Università degli Studi di Milano Bicocca, Monza, Italy

  • Pediatric Hemato-Oncology Department, Fondazione MBBM, University of Milano Bicocca, Monza, Italy

  • Cell Factory, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy

  • Bone Marrow Transplant Center, Institute for Maternal and Child Health - IRCCS Burlo Garofolo, Trieste, Italy

  • Policlinico San Matteo, Pavia, Pavia, ITA

  • IRCCS Fondazione Policlinico San Matteo, Pavia, Pavia, Italy

  • Pediatric Hematology/Oncology, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy

  • Department of Diagnostic Medicine, Clinical and Experimental Pharmacokinetics Unit, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy

  • Università degli Studi di Milano-Fondazione MBBM, Monza, Italy

  • Department of Pediatrics, University of Milano - Bicocca, Fondazione MBBM, Monza, Italy

  • Clinica Pediatrica Università Milano Bicocca/Fondazione MBBM, Monza, Italy

  • Pediatric Clinic - Hemato-Oncology Department, University of Milano-Bicocca, MBBM Fundation c/o San Gerardo Hospital, Monza, Italy

  • Pediatric Immunohematology and Bone Marrow Transplantation Unit, San Raffaele Scientific Institute, Milan, Italy

  • Institute of Maternal and Child Health, Trieste, Italy

Locations

  • Italy

Companies

  • N/A

Study Components

Therapeutic Area

  • N/A

Disease

  • N/A

Biomarkers

  • N/A

Drug/Treatment

  • treosulfan

  • Ovastat

  • Busulfan

Outcome

  • N/A


Study Design

  • Efficacy

  • Pharmacokinetics

  • Pharmacodynamics

  • Multicenteric

  • Prospective

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A