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Gili Kenet
Beatrice Nolan
Tadashi Matsushita
Guy Young
Ting Quan
Viridiana Cano
Christian Sussebach
Shauna Andersson
Baisong Mei
Marion Afonso
Kaan Kavakli
Our Lady's Children's Hospital, Dublin, Ireland
Sheba Medical CENTER, Ramat Gan, Israel
Ege University Children's Hospital, Clinic of Children's Health and Diseases, Division of Pediatric Hematology, Izmir, Turkey
TEL AVIV UNIVERSITY, Tel Aviv, Israel
Keck School of Medicine, University of Southern California, Los Angeles, CA
Children's Hospital Los Angeles, University of Southern California, Los Angeles, CA
Department of Transfusion Medicine, Nagoya University Hospital, Nagoya, Japan
Ireland
United States
Germany
Israel
Turkey
China
Japan
France
N/A
Blood/haematological Diseases
Hemophilia
N/A
N/A
N/A
Open Label
Multinational
Multicenteric
III
N/A
N/A
N/A