// App-Quantinova.ai

: Multiplex CRISPR/Cas9 Gene Editing in Human Stem Cells to Model Clonal Competition in GATA2 Deficiency

Researchers

Presenter

  • Damia Romero-Moya

Principal Investigators

  • Oskar Marin-Bejar

  • Maximiliano Distefano

  • Joan Pera

  • Julio Castaño

  • Jessica Gonzalez

  • Lili Kotmayer

  • Csaba Bodor

  • Albert Catala

  • Marcin W Wlodarski

  • Anna Bigas

  • Alessandra Giorgetti

Medical Centers

  • Instituto de Salud Carlos III, Biomedical Network Research Centre on Rare Diseases, Madrid, Spain

  • Department of Pathology and Experimental Therapeutics, Faculty of Medicine and Health Sciences, Barcelona University, Barcelona, Spain

  • Regenerative Medicine Program, Institut d'Investigació Biomèdica de Bellvitge (IDIBELL), Hospitalet De Llobregat, Spain

  • Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN

  • Cancer Research Program, Institut Hospital del Mar d'Investigacions Mèdiques, CIBERONC, Hospital del Mar, Barcelona, Spain

  • Department of Hematology and Oncology, Institut de Recerca Sant Joan de Déu, Hospital Sant Joan de Deu, Barcelona, Spain

  • HCEMM-SE Momentum Molecular Oncohematology Research Group, st Department of Pathology and Experimental Cancer Research, Semmelweis University, Budapest, Hungary

  • Josep Carreras Research Institute (IJC), Badalona, Spain

  • Immunotherapy Unit, Banc de Sang i Teixits, Barcelona, Spain

Locations

  • Spain

  • United States

  • Hungary

Companies

  • N/A

Study Components

Therapeutic Area

  • Oncology (ONC)

Disease

  • Myelodysplastic Syndrome

  • Acute myelocytic leukemia

Biomarkers

  • Cluster of Differentiation 19

  • Cluster of differentiation 45

Drug/Treatment

  • N/A

Outcome

  • N/A


Study Design

  • N/A

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A