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: Deciphering Treatment Patterns in Non-Severe Aplastic Anemia: An International Observational Study

Researchers

Presenter

  • Bruno Fattizzo

Principal Investigators

  • Carmelo Gurnari

  • Giulio Cassanello

  • Marta Bortolotti

  • Hussein Awada

  • Sabrina Giammarco

  • Dario Consonni

  • Simona Sica

  • Shreyans Gandhi

  • Roochi Trikha

  • Jaroslaw P. Maciejewski

  • Austin Kulasekararaj

  • Wilma Barcellini

Medical Centers

  • Department of Oncology and Oncohaematology, University of Milan, Milan, Italy

  • Haematological Medicine, King's College Hospital NHS Trust, London, United Kingdom

  • University of Milano, Milan, ITA

  • Dipartimento di Diagnostica per Immagini, Radioterapia Oncologica ed Ematologia, Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy

  • Hematology Unit, Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Milan, Italy

  • King's College Hospital, National Institute for Health and Care Research/Wellcome King's Clinical Research Facility, London, United Kingdom

  • Department of Translational Hematology and Oncology Research, Taussig Cancer Institute, Cleveland Clinic Foundation, Cleveland, OH

  • Translational Hematology and Oncology Research, Cleveland Clinic Foundation/ Taussig Cancer Institute, Cleveland, OH

  • Fondazione Policlinico A. Gemelli IRCCS, Roma, Italy; Istituto di Ematologia, Università Cattolica del Sacro Cuore, Roma, Italy, Roma, Italy

  • Hematology Unit, Pathophysiology of Anemias Unit, Foundation IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Milan, Italy

  • King's College Hospital, London, United Kingdom

  • Università degli studi di Milano, Milano, Italy

Locations

  • Italy

  • United Kingdom

  • United States

Companies

  • N/A

Study Components

Therapeutic Area

  • Pulmonary/Respiratory Diseases

  • Cardiovascular (CVS)

  • Blood/haematological Diseases

Disease

  • Thrombocytopenia

  • Aplastic anemia

  • Neutropenia

  • Venous thrombosis

  • Anemia

Biomarkers

  • MPL proto-oncogene, thrombopoietin receptor

  • Calreticulin

  • N-Acylethanolamine acid amidase

  • E1A Binding Protein P300

  • E3 ubiquitin-protein ligase CBL

  • Enhancer of zeste homolog 2

  • DNA methyltransferase 3 alpha

  • ETV6-RUNX1

  • GTPase Nras

  • Tet methylcytosine dioxygenase 2

  • Neurofibromatosis type 1

  • Red Blood Cells

Drug/Treatment

  • Oraprine

  • Alemtuzumab

  • Eltrombopag

  • cyclosporin

  • Daclizumab

  • EP300

  • EZH2

Outcome

  • N/A


Study Design

  • Observational

  • Multinational

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A