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: Current Use of Androgens in Bone Marrow Failure Disorders: A Report from the Severe Aplastic Anemia Working Party (SAAWP) of the European Society of Blood and Marrow Transplantation (EBMT)

Researchers

Presenter

  • Simona Pagliuca

Principal Investigators

  • Dirk-Jan Eikema

  • Brian Piepenbroek

  • Raheel Iftikhar

  • Tariq Mahmood Satti

  • Morag Griffin

  • Marica Laurino

  • O. Alphan Kupesiz

  • Yives Bertrand

  • Bruno Fattizzo

  • Ibrahim Yakoub-Agha

  • Mahmoud Aljurf

  • Paola Corti

  • Erika Massaccesi

  • Bruno Lioure

  • Marisa Calabuig

  • Matthias Klammer

  • Emel Unal

  • Depei Wu

  • Patrice Chevallier

  • Edouard Forcade

  • John A. Snowden

  • Hakan Ozdogu

  • Antonio Risitano

  • Regis Peffault de Latour

Medical Centers

  • Centre Hospitalier Universitaire de Strasbourg, Strasbourg, France

  • Pediatric Hemato-Oncolgy, Fondazione MBBM/ASST-Monza, University of Milano-Bicocca, Monza, Italy

  • Department of Clinical Hematology, CHRU Nancy, Vandœuvre-lès-Nancy, France

  • Institute of Pediatric Hematology and Oncology, Civil Hospital of Lyon - Claude Bernard University, Lyon, France

  • Hematology Department, Nantes University Hospital, Nantes, France

  • EBMT Statistical Unit, Leiden, Netherlands

  • Hospital Clínico de Valencia, Valencia, Spain

  • IRCSS Istituto Giannina Gaslini, Genoa, Italy

  • UO ematologia e terapie cellulari, IRCCS Ospedale Policlinico San martino, Genova, Italy

  • EBMT Leiden Study Unit, Leiden, Netherlands

  • Assistance Publique-Hôpitaux de Paris, Saint-Louis Hospital, Université Paris Cité, Paris, France

  • Oncology Center, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

  • Sheffield University Teaching Hospitals, Sheffield, United Kingdom

  • King's College Hospital, National Institute for Health and Care Research/Wellcome King's Clinical Research Facility, London, United Kingdom

  • Dipartimento di Oncologia e Emato-Oncologia, Fondazione IRCCS Ca’ Granda - Ospedale Maggiore Policlinico, Milano, Italy

  • CNRS UMR IMoPa, Biopôle de l'Université de Lorraine, Vandœuvre-lès-Nancy, France

  • Service d'Hématologie Clinique et Thérapie Cellulaire, CHU Bordeaux, Hôpital Haut-Leveque, Bordeaux, France

  • Hematology Department, Akdeniz University Medical School, Antalya, Turkey

  • Armed Forces Bone MarrowTransplant Centre, Rawalpindi, Pakistan

  • Division of Pediatric Hematology/Oncology, Ankara University Faculty of Medicine, Department of Pediatrics - Division of Pediatric Hematology-Oncology, Ankara, Turkey., Istanbul, Turkey

  • National Clinical Research Center for Hematologic Diseases, Jiangsu Institute of Hematology, The First Affiliated Hospital of Soochow University, Institute of Blood and Marrow Transplantation of Soochow University, Suzhou, China

  • Centre Hospitalier Universitaire de Lille LIRIC, INSERM U, Université de Lille, Lille, France

  • St. George's University Hospital, London, United Kingdom

  • Hematology Division, BMT Unit, Haemaology Reserach Laboratory, Training & Medical, Baskent University Hospital, Adana, Turkey

  • St James's University Hospital, Sheffield, United Kingdom

  • Hematology and Hematopoietic Transplantation, AORN S. Giuseppe Moscati Avellino, Avellino, Italy

  • French Reference Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Paris, France

Locations

  • France

  • China

  • Italy

  • United Kingdom

  • Netherlands

  • Turkey

  • Pakistan

  • Saudi Arabia

  • Spain

Companies

  • N/A

Study Components

Therapeutic Area

  • Genetic Disorder

  • Blood/haematological Diseases

Disease

  • Dyskeratosis congenita

  • Aplastic anemia

  • Fanconi anemia

  • Anemia

Biomarkers

  • Hematocrit

  • Tyrosine 3-Monooxygenase/Tryptophan 5-Monooxygenase Activation Protein Epsilon

Drug/Treatment

  • Cyclosporine eent

  • oxymetholone

  • nandrolone

  • Androgen Tear

  • Danazol

Outcome

  • N/A


Study Design

  • Cohort

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A