// App-Quantinova.ai

: Modeling Human Paroxysmal Nocturnal Hemoglobinuria Via CRISPR/Cas9 HSPC Gene Editing in Non-Human Primate

Researchers

Presenter

  • Taehoon Shin

Principal Investigators

  • Eun Jung Baek

  • Marcus A.F. Corat

  • Shirley Chen

  • Robert E. Donahue

  • Kyung-Rok Yu

  • Cynthia E. Dunbar

Medical Centers

  • Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institute of Health, BETHESDA, MD

  • Department of Laboratory Medicine, College of Medicine, Department of Translational Medicine, Graduate School of Biomedical Science and Engineering, Hanyang University Guri Hospital, Guri-si, Gyeonggi-do, Korea, Republic of (South)

  • Multidisciplinary Center for Biological Research, State University of Campinas - Unicamp, Campinas, Brazil

  • Hematology Branch, National Heart Lung and Blood Institute, National Institutes of Health, Bethesda, MD

Locations

  • United States

  • Republic of South Korea

  • Brazil

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

  • Pulmonary/Respiratory Diseases

  • Cardiovascular (CVS)

Disease

  • Paroxysmal nocturnal hemoglobinuria

  • Venous thrombosis

Biomarkers

  • Cluster of Differentiation 14

  • Cluster of Differentiation 24

  • Cluster of Differentiation 34

Drug/Treatment

  • N/A

Outcome

  • N/A

Study Design

  • N/A

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A

Copyright © 2026. QuantiNova All rights reserved