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1687 : Trial in Progress: A Real-World Cohort Study Reporting Patient Profiles, Clinical Outcomes, and Unmet Medical Need of Patients with Paroxysmal Nocturnal Hemoglobinuria Treated with Eculizumab in the Essen Center in Germany

Researchers

Presenter

  • Katharina Versmold

Principal Investigators

  • Carina Raiser

  • Imi Faghmous

  • Pablo Katz

  • Aijing Shang

  • Tao Xu

  • Alexander Rth

Medical Centers

  • Department of Dermatology, University Hospital, University Duisburg-Essen, Essen, Germany

  • F. Hoffmann-La Roche Ltd., Basel, Switzerland

  • Department of Dermatology, University Hospital, University Duisburg-Essen, Essen, Germany

Locations

  • Germany

  • Switzerland

Companies

  • F. Hoffmann-La Roche

Study Components

Therapeutic Area

  • Blood/haematological Diseases

Disease

  • Paroxysmal nocturnal hemoglobinuria

  • Aplastic anemia

  • Renal insufficiency

  • Venous thrombosis

  • Anemia

Biomarkers

  • Lactate dehydrogenase

Drug/Treatment

  • Eculizumab

Outcome

  • N/A


Study Design

  • Cohort

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A