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: Adeno-Associated Virus-Mediated Factor H Gene Therapy in a Murine Model of Complement-Dependent Thrombotic Microangiopathy and Systemic Thrombophilia

Researchers

Presenter

  • DaisukeIto

Principal Investigators

  • HangsooKim

  • DamodaraGullipalli

  • YoshiyasuUeda

  • TakashiMiwa

  • SayakaSato

  • LinZhou

  • MatthewPalmer

  • JunXie

  • GuangpingGao

  • Wen-ChaoSong

Medical Centers

  • University of Pennsylvania, Philadelphia, Pennsylvania, United States

  • University of Pennsylvania, Philadelphia, Pennsylvania, United States

  • University of Massachusetts Medical School, Worcester, Massachusetts, United States

Locations

  • United States

Companies

  • N/A

Study Components

Therapeutic Area

  • Musculoskeletal

  • Pulmonary/Respiratory Diseases

  • Blood/haematological Diseases

  • Cardiovascular (CVS)

Disease

  • Thrombotic microangiopathy

  • Venous thrombosis

Biomarkers

  • N/A

Drug/Treatment

  • N/A

Outcome

  • N/A


Study Design

  • Randomized

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A