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Karolina Komorowska
Hanna K.A Mikkola
Jonas Larsson
Mattias Magnusson
Molecular Medicine and Gene Therapy, Lund Stem Cell Center, Lund University, Lund, Sweden
University of California, Los Angeles, Los Angeles, CA
United States
Sweden
N/A
Central Nervous System (CNS)
Genetic Disorder
Acute lymphoblastic leukemia
Spinocerebellar ataxia 1
Proto-oncogene tyrosine-protein kinase ROS
Endothelial PAS Domain Protein 1
Glomeruloid microvascular proliferation
N/A
N/A
N/A
NA
N/A
N/A
Interim