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L.-A. Bissell
B. Erhayiem
E. Hensor
G. Fent
J.P. Greenwood
S. Plein
J. Andrews
M.H. Buch
University of Leeds, Leeds, United Kingdom
United Kingdom
N/A
Genetic Disorder
Central Nervous System (CNS)
Heart muscle disease
Diabetes
Mental retardation, X-linked, syndromic, 15
Carboxypeptidase B1
Albumin/creatinine
Cyclophosphamide
Cyclophosphamide Injection
N/A
N/A
NA
N/A
N/A
Interim