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R. Altman
A. Gibofsky
D. Parenti
C. Young
David Geffen School of Medicine, University of California Los Angeles, Los Angeles, CA
Hospital for Special Surgery, New York, NY.
United States
iROKO Partners Ltd
Genetic Disorder
Musculoskeletal
Deep vein thrombosis
Constipation
C1 Inhibitor Deficiency
Venous thrombosis
Anxiety
Short stature, onychodysplasia, facial dysmorphism, and hypotrichosis
N/A
Indomethacin
Celecoxib
ALT-210
N/A
N/A
III
N/A
N/A
Interim