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3718 : Insights Into The Natural History Of Paroxysmal Nocturnal Hemoglobinuria (PNH): Analysis Of The Presenting Clinical, Haematological and Flow Cytometric Features Of 705 Patients Leads To Improved Classification and Prediction Of Clinical Course

Researchers

Presenter

  • Stephen John Richards

Principal Investigators

  • Richard Kelly

  • Anita Hill

  • Anita Dickinson

  • Fiona Cullen

  • Jane Shingles

  • Matthew Cullen

  • Peter Hillmen

Medical Centers

  • The Leeds Teaching Hospitals, St. James Institute of Oncology, Leeds, United Kingdom

  • St. James's University Hospital, Leeds, United Kingdom

Locations

  • United Kingdom

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

Disease

  • Paroxysmal nocturnal hemoglobinuria

  • Myeloid neoplasms

  • Aplastic anemia

  • Fanconi anemia

  • Myelodysplastic Syndrome

  • Venous thrombosis

  • Anemia

Biomarkers

  • Glycosylphosphatidylinositol

  • Mean corpuscular volume

  • White Blood Cell

  • Red Blood Cells

Drug/Treatment

  • Eculizumab

Outcome

  • N/A


Study Design

  • N/A

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • Interim