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Seiichi Odate
Shuang Yan
Veronica Veschi
Norris Lam
Zhihui Liu
Carol J. Thiele
National Cancer Institute, Bethesda, MD
United States
N/A
Genetic Disorder
Musculoskeletal
Neuroblastoma
Solid malignancies
Short stature, onychodysplasia, facial dysmorphism, and hypotrichosis
cMYC
Janus kinase
Tetracycline
Cisplatin
AZD-9150
N/A
N/A
I/II
N/A
N/A
N/A